Rovanersen
Cat. No.:YN380432
产品名称: | Rovanersen |
CAS No.: | 2072901-32-5 |
Chemical Name: | |
Synonyms: | WVE-120101 |
分子量: | 暂无 |
分子式: | 暂无 |
SMILES: | 暂无 |
存储: | Please store the product under the recommended conditions in theCertificate of Analysis. |
运输: | Room temperature in continental US; may vary elsewhere. |
产品描述: | Rovanersen (WVE-120101) 是一种反义寡核苷酸,通过特异靶向huntingtin(HTT)基因的突变mRNA拷贝,而不影响正常的HTT基因的mRNA,从而防止有缺陷的huntingtin蛋白的产生。Rovanersen 可用于亨廷顿病的研究。 |
IC50和靶点: | |
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Clinical Trial: | |
Solvent & Solubility: |